 Home > Active Ingredient News > Study of Nervous System > Astellas' gene therapy takes another hit

Astellas' gene therapy takes another hit

 Last Update: 2022-05-22
 Source: Internet
 Author: User

Tags

hela cells uses

il 2 function

Search more information of high quality chemicals, good prices and reliable suppliers, visit www.echemi.com

Duchenne muscular dystrophy (DMD) is the most common type of progressive muscular dystrophy, with progressive and lethal features

Duchenne muscular dystrophy (DMD) is caused by the absence or loss of function of dystrophin

The gene encoding dystrophin is located at Xp21.

Japanese pharmaceutical company Astellas has disclosed that it will discontinue its AT702, AT751 and AT753 gene therapy programs for Duchenne muscular dystrophy (DMD) based on recent preclinical study data

The company's gene therapy approach for DMD uses an AAV vector encoding a modified U7 snRNA to deliver an antisense sequence designed to induce cells to skip the erroneous or misplaced genetic code in the dystrophin gene, thereby restoring functional dystrophin Production of atrophin

Original source:

https://firstwordpharma.

https://firstwordpharma.
com/story/5554133 https://firstwordpharma.
com/story/5554133

Leave a comment here

This article is an English version of an article which is originally in the Chinese language on echemi.com and is provided for information purposes only. This website makes no representation or warranty of any kind, either expressed or implied, as to the accuracy, completeness ownership or reliability of the article or any translations thereof. If you have any concerns or complaints relating to the article, please send an email, providing a detailed description of the concern or complaint, to service@echemi.com. A staff member will contact you within 5 working days. Once verified, infringing content will be removed immediately.

Related Products

Pregabalin Crystal CAS 148553-50-8 Lyrica Powder 99.0% White Powder Mobelbiochem

CAS No.: 148553-50-8

Pharmacy Grade

$35.00/KG FOB

Pregabalin Powder CAS No. 148553-50-8

CAS No.: 148553-50-8

Pharmacy Grade

$120-150/KG FOB

Oversea Warehuse Stock Free Customs-clearance Pregabalin Powder (CAS 148553-50-8)

CAS No.: 148553-50-8

Pharmacy Grade

$120-150/KG FOB

Hot Tags

united states jobs(223)

jobs united states(236)

1 year treasury(277)

1 year subscription(296)

announcements today(81)

80 20 company(94)

united states logo(227)

single use technology(195)

healthy food name(42)

ups united states(221)

Hot Articles

The source of this page with content of products and services is from Internet, which doesn't represent ECHEMI's opinion. If you have any queries, please write to service@echemi.com. It will be replied within 5 days.

Moreover, if you find any instances of plagiarism from the page, please send email to service@echemi.com with relevant evidence.